From Height to Health: Changing the Conversation in Achondroplasia
At 澳门正规博彩十大排行平台, we’re committed to deepening our understanding of achondroplasia and taking a holistic approach to support this community.
Supporting Women at 澳门正规博彩十大排行平台: An Interview with the Co-Chairs of Our Women’s Leadership Development Group
As we recognize International Women’s Day and Women’s History Month in March, we caught up with Carolina Amador and Paola Torre to discuss what they’re focused on as they step into leadership roles with our women’s ERG.
Caring for Children with Achondroplasia: An Interview with Dr. Ciara McDonnell
Dr. McDonnell, a renowned pediatric endocrinologist, shares her perspective about the current care experience for families affected by achondroplasia, how care has evolved and what makes her optimistic about the future.
Read More read more ⌃Targeting the Underlying Genetic Causes of Heart Disease
澳门正规博彩十大排行平台 researchers are leveraging the company’s expertise in translating genetic discoveries into potentially transformative medicines to address the root causes of certain forms of cardiovascular disease.
RARE Scholars Program Provides Support to College Students Living with Genetic Conditions
The program was created to support U.S. college students living with one of four rare genetic conditions who have demonstrated exceptional leadership and engagement in school and community activities.
澳门正规博彩十大排行平台 Teams Use Genetic Expertise and Computational Tools to Target More Common Conditions
For geneticist Daniel Gaffney, becoming an expert in how genes influence human health was not enough. His drive to improve lives with this knowledge led him to 澳门正规博彩十大排行平台, where he found a shared commitment to translating scientific advances into medicines that solve genetic problems. Since joining the company earlier this year, Dan has helped its […]
Clinical Trials
Our thoughtful approach to clinical trial design enables us to move fast and efficiently while protecting the safety of our patients.
Learn More about our clinical trials ⌃